Everolimus for cardiac rhabdomyomas in children with tuberous sclerosis. The ORACLE study protocol (everOlimus for caRdiac rhAbdomyomas in tuberous sCLErosis): a randomised, multicentre, placebo-controlled, double-blind phase II trial
Stelmaszewski, Erica V.; Parente, Daniella B.; Fariña, Alberto; Stein, Anna; Gutiérrez, Anthony; Raquelo Menegassio, Antonio F.; Manterola, Carla; de Sousa, Carolina F.; Víctor, Carolina; Maki, Dina; Morón, Elías M.; de Abrantes, Fabiano F.; Iqbal, Fátima; Camacho Vilchez, Jazmín; Jiménez Pavón, Joanna; Polania, Juan P.; Thompson, Lorenzo; Bonanato, Lygia; Diebold, Matthias; Da Silva, Maria V. C. P.; Nashwan, Mariam W. J.; Galvani, Marianna A. G.; Idris, Osama E. A.; Danos, Pierina; Ortiz López, Rocío; Mahmoud, Rofida A. A.; Gresse, Sergio Jr.; Loss, Karla L. (Cambridge University Press, 2020)